English
English Indonesia Türkçe Deutsch Español Português Pусский Français Italiano Nederlands Polski العربية ไทย Tiếng Việt 繁體中文 简体中文 日本語 한국어

#adascid search results

UCLATDG's profile picture. UCLA Technology Development Group serves as the tech transfer office for the university. Our team bridges academic research to commercialization.
UCLA TDG
 @UCLATDG
Oct 14

#RarityPBC secures exclusive license from @UCLATDG for advancing lifesaving therapy tdg.ucla.edu/rarity-pbc-sec… #ADASCID #bubblebaby #ucla #lifesaving #genetherapy

UCLATDG's tweet image. #RarityPBC secures exclusive license from @UCLATDG for advancing lifesaving therapy tdg.ucla.edu/rarity-pbc-sec… #ADASCID #bubblebaby #ucla #lifesaving #genetherapy
0
0
2
0
55
Kohn_Lab's profile picture. Our mission is to treat patients suffering from primary immunodeficiency diseases with hematopoietic stem cell gene therapy.🩸🦠✂️🧬⛑: tweets from lab members.
The Kohn Lab UCLA
 @Kohn_Lab
May 18, 2022

As Dr. Donald Kohn shares his work on ADA-SCID gene therapy, we want to remind that this clinical trial has resumed with the support of @CIRMnews . We ask for your continuous support as we treat more patients with #ADASCID. #ASGCT2022

Kohn_Lab's tweet image. As Dr. Donald Kohn shares his work on ADA-SCID gene therapy, we want to remind that this clinical trial has resumed with the support of @CIRMnews . We ask for your continuous support as we treat more patients with #ADASCID. #ASGCT2022
0
3
19
0
0
eerr_es's profile picture. Web dedicada a la información sobre enfermedades raras.
EnfermedadesRaras.es
 @eerr_es
Oct 17

Una novedosa terapia génica salva la vida de 62 'niños burbuja' portadores de una enfermedad rara #ADASCID antena3.com/noticias/salud… a través de @A3Noticias

eerr_es's tweet image. Una novedosa terapia génica salva la vida de 62 'niños burbuja' portadores de una enfermedad rara #ADASCID antena3.com/noticias/salud… a través de @A3Noticias
0
0
0
0
65
_timos_'s profile picture. BioPharma & HealthTech Competitive Strategy & Insights | Digital & AI Solutions | Gene & Cell Therapy | Vaccines
Dr Timos Papagatsias
 @_timos_
Oct 24

LucidQuest Updates > Public Health Video Recap—October 24, 2025 dlvr.it/TNsD2v #BioPharmaandTechNews #PublicHealthNews #ADASCID Comment below!

_timos_'s tweet image. LucidQuest Updates > Public Health Video Recap—October 24, 2025 dlvr.it/TNsD2v #BioPharmaandTechNews #PublicHealthNews #ADASCID Comment below!
0
0
0
0
9
Inside_PM's profile picture. Exclusive news, features, and analysis on the research, tools, regulations, and applications driving precision medicine. From the publisher of @GENBio
Inside Precision Medicine
 @Inside_PM
May 12, 2021

2 to 3 Years Later, Gene Therapy Still Helping Patients with #ADASCID. 48 of 50 children who were provided a #genetherapy for the disease ADA-SCID retain replenished immune system function two to three years after receiving their treatment. Read more: ow.ly/DxUL50EL8Fu

Inside_PM's tweet image. 2 to 3 Years Later, Gene Therapy Still Helping Patients with #ADASCID. 48 of 50 children who were provided a #genetherapy for the disease ADA-SCID retain replenished immune system function two to three years after receiving their treatment. Read more: ow.ly/DxUL50EL8Fu
0
4
9
0
0
SpringerIME's profile picture. Springer Health+ IME, providing independent medical education in Neurology, Diabetes, Oncology, Rare Diseases, Endocrinology, and Paediatrics.
Springer Health+ IME
 @SpringerIME
May 13, 2020

NEW article available Support for using E coli-expressed PEG-ADA for ADA-SCID Read here bit.ly/t-ADA-SCID-art… #ADASCID #RareDisease #Ecoli #infants #PEG #EscherichiaColi

SpringerIME's tweet image. NEW article available Support for using E coli-expressed PEG-ADA for ADA-SCID Read here bit.ly/t-ADA-SCID-art… #ADASCID #RareDisease #Ecoli #infants #PEG #EscherichiaColi
0
0
2
0
0
SpringerIME's profile picture. Springer Health+ IME, providing independent medical education in Neurology, Diabetes, Oncology, Rare Diseases, Endocrinology, and Paediatrics.
Springer Health+ IME
 @SpringerIME
Sep 10, 2018

Newborn Screening for ADA-SCID, A new interactive patient case study from Professor Chiara Azzari. Test your knowledge ada-scid.online/case-studies/n… #diagnose #ADASCID #immunology #RARE #RareDisease #showyourrare #celltherapy #genetherapy #primaryimmunodeficiency #Paediatrics #PID

SpringerIME's tweet image. Newborn Screening for ADA-SCID, A new interactive patient case study from Professor Chiara Azzari. Test your knowledge ada-scid.online/case-studies/n… #diagnose #ADASCID #immunology #RARE #RareDisease #showyourrare #celltherapy #genetherapy #primaryimmunodeficiency #Paediatrics #PID
0
2
1
1
0
SpringerIME's profile picture. Springer Health+ IME, providing independent medical education in Neurology, Diabetes, Oncology, Rare Diseases, Endocrinology, and Paediatrics.
Springer Health+ IME
 @SpringerIME
Feb 21, 2020

New article available: Chest radiographs may help diagnose ADA-SCID early Read here bit.ly/t-ADA-SCID-art… #RareDiseases #ADASCID #GeneTherapy #rare #Pediatrics #Immunology

SpringerIME's tweet image. New article available: Chest radiographs may help diagnose ADA-SCID early Read here bit.ly/t-ADA-SCID-art… #RareDiseases #ADASCID #GeneTherapy #rare #Pediatrics #Immunology
0
1
0
0
0
SpringerIME's profile picture. Springer Health+ IME, providing independent medical education in Neurology, Diabetes, Oncology, Rare Diseases, Endocrinology, and Paediatrics.
Springer Health+ IME
 @SpringerIME
Mar 22, 2018

Medical education needs you! Please visit New Horizons in the Management of ADA-SCID & share your feedback in a very short survey #diagnose #ADASCID #immunology #RareDisease #showyourrare #celltherapy #genetherapy #primaryimmunodeficiency #Paediatrics #PID bit.ly/2rXEmiP

SpringerIME's tweet image. Medical education needs you! Please visit New Horizons in the Management of ADA-SCID & share your feedback in a very short survey #diagnose #ADASCID #immunology #RareDisease #showyourrare #celltherapy #genetherapy #primaryimmunodeficiency #Paediatrics #PID bit.ly/2rXEmiP
0
1
0
0
0
EKFStiftung's profile picture. Die EKFS widmet sich der Förderung medizinischer Forschung und unterstützt medizinisch-humanitäre Projekte. Impressum: https://t.co/ETxaZq2WIJ
Else Kröner-Fresenius-Stiftung
@EKFStiftung
Jun 8, 2020

#EKFSprize20 winner Alessandro Aiuti has made major contributions to a gene therapy for the rare immune disease #ADASCID. Approved as a pharmaceutical remedy in Europe, it is considered one of the most important results of #GeneTherapy development worldwide. #EKFS #healthcare

EKFStiftung's tweet image. #EKFSprize20 winner Alessandro Aiuti has made major contributions to a gene therapy for the rare immune disease #ADASCID. Approved as a pharmaceutical remedy in Europe, it is considered one of the most important results of #GeneTherapy development worldwide. #EKFS #healthcare
0
0
2
1
0
SpringerIME's profile picture. Springer Health+ IME, providing independent medical education in Neurology, Diabetes, Oncology, Rare Diseases, Endocrinology, and Paediatrics.
Springer Health+ IME
 @SpringerIME
Jan 2, 2019

Extra Immunological Aspects of ADA-SCID. Test your knowledge with this interactive patient case study from Dr Robert Sokolic #diagnose #ADASCID #immunology #RARE #RareDisease #celltherapy #genetherapy #primaryimmunodeficiency #Paediatrics #PID #skincancer bit.ly/2CKQTOu

SpringerIME's tweet image. Extra Immunological Aspects of ADA-SCID. Test your knowledge with this interactive patient case study from Dr Robert Sokolic #diagnose #ADASCID #immunology #RARE #RareDisease #celltherapy #genetherapy #primaryimmunodeficiency #Paediatrics #PID #skincancer bit.ly/2CKQTOu
0
0
1
0
0
eClinicalMed's profile picture. Gold open access clinical journal, part of @TheLancet Discovery Science, influencing clinical practice and strengthening health. IF: 10·0; CiteScore: 17·0.
eClinicalMedicine – The Lancet Discovery Science
 @eClinicalMed
Feb 22, 2019

Packed room at #TCTM19 for the President’s Symposium on Cell and Gene Therapy: Next Big Challenges. Outstanding talks by Luigi Naldini, David Williams and Don Kohn. (slide from D. Kohn on #ADASCID #genetherapy)

eClinicalMed's tweet image. Packed room at #TCTM19 for the President’s Symposium on Cell and Gene Therapy: Next Big Challenges. Outstanding talks by Luigi Naldini, David Williams and Don Kohn. (slide from D. Kohn on #ADASCID #genetherapy)
0
1
0
0
0
orchard_tx's profile picture. Dedicated to transforming the lives of patients with inherited diseases through innovative gene therapy.
Orchard Therapeutics - U.S.
 @orchard_tx
Jun 19, 2020

In 2012, Orchard’s scientific founders treated the first patient in a clinical trial of an investigational ex vivo autologous #genetherapy to treat #ADASCID. Learn more about gene therapy’s history: bit.ly/2QYkATg

orchard_tx's tweet image. In 2012, Orchard’s scientific founders treated the first patient in a clinical trial of an investigational ex vivo autologous #genetherapy to treat #ADASCID. Learn more about gene therapy’s history: bit.ly/2QYkATg
0
2
4
0
0
alliancerm's profile picture. ARM champions the benefits of engineered cell therapies and genetic medicines for patients, healthcare systems, and society.
Alliance for Regenerative Medicine (ARM)
 @alliancerm
Jul 27, 2021

The EU’s Cross Border Healthcare Directive often doesn’t work for patients trying to access life-changing #ATMPs. Of 14 #ADASCID patients referred to receive the #genetherapy Strimvelis, only 6 have been treated. The therapy is available only in a treatment center in Milan. (1/2)

alliancerm's tweet image. The EU’s Cross Border Healthcare Directive often doesn’t work for patients trying to access life-changing #ATMPs. Of 14 #ADASCID patients referred to receive the #genetherapy Strimvelis, only 6 have been treated. The therapy is available only in a treatment center in Milan. (1/2)
1
0
6
0
0
humantechnopole's profile picture. The next-generation #lifesciences institute advancing human health through basic research and collaboration.
Human Technopole
 @humantechnopole
Nov 20, 2023

Current therapies address immune issues of the #ADASCID rare genetic disorder, but gaps persist in tackling its neurocognitive challenges. With our @harschnitz and @Telethonitalia's support, we'll use #organoid models to identify new therapeutic targets youtu.be/TYBAtoZekpU

humantechnopole's tweet card. Our Research on the Neuropathology of ADA-SCID with Oliver Harschnitz

youtube.com

YouTube

Our Research on the Neuropathology of ADA-SCID with Oliver Harschnitz

Source: youtube.com
0
1
2
1
885
historyatnih's profile picture. Official account of the Office of NIH History and Stetten Museum, National Institutes of Health. We inform, document, and preserve the history of NIH.
NIH History Office
 @historyatnih
Jun 11, 2024

Did you know the first successful gene therapy was done @NIH? Before gene therapy, #ADASCID patients had to receive regular doses of the ADA enzyme, like those pictured here. This recent donation of vials helps us tell the important history of gene therapy.

historyatnih's tweet image. Did you know the first successful gene therapy was done @NIH? Before gene therapy, #ADASCID patients had to receive regular doses of the ADA enzyme, like those pictured here. This recent donation of vials helps us tell the important history of gene therapy.
0
0
2
0
85
bobby_gaspar's profile picture. Professor @UCL @GreatOrmondSt talking about gene therapy, primary immunodeficiency, SCID, rare diseases. Politics and sports enthusiast. My views are my own.
Prof. Bobby Gaspar
 @bobby_gaspar
Sep 12, 2019

Huge thanks to @The_MRC for the translational funding that helped develop this #GeneTherapy for #ADASCID at @UCLchildhealth and @GreatOrmondSt Couldn’t have done it without this funding....thank you!

The_MRC's profile picture. UKRI MRC is dedicated to improving human health since 1913. Part of UK Research and Innovation @UKRI_News.
Medical Research Council
 @The_MRC
Sep 12, 2019

How Prof @bobby_gaspar & his team @UCL @GreatOrmondSt used MRC funding to develop a new gene therapy for a rare inherited immune disorder (see case study) 👉 mrc.io/31jvupa

1
1
4
0
0
1
4
27
0
0
_timos_'s profile picture. BioPharma & HealthTech Competitive Strategy & Insights | Digital & AI Solutions | Gene & Cell Therapy | Vaccines
Dr Timos Papagatsias
 @_timos_
Oct 24

LucidQuest Updates > Public Health Video Recap—October 24, 2025 dlvr.it/TNsD2v #BioPharmaandTechNews #PublicHealthNews #ADASCID Comment below!

_timos_'s tweet image. LucidQuest Updates > Public Health Video Recap—October 24, 2025 dlvr.it/TNsD2v #BioPharmaandTechNews #PublicHealthNews #ADASCID Comment below!
0
0
0
0
9
eerr_es's profile picture. Web dedicada a la información sobre enfermedades raras.
EnfermedadesRaras.es
 @eerr_es
Oct 17

Una novedosa terapia génica salva la vida de 62 'niños burbuja' portadores de una enfermedad rara #ADASCID antena3.com/noticias/salud… a través de @A3Noticias

eerr_es's tweet image. Una novedosa terapia génica salva la vida de 62 'niños burbuja' portadores de una enfermedad rara #ADASCID antena3.com/noticias/salud… a través de @A3Noticias
0
0
0
0
65
UCLATDG's profile picture. UCLA Technology Development Group serves as the tech transfer office for the university. Our team bridges academic research to commercialization.
UCLA TDG
 @UCLATDG
Oct 14

#RarityPBC secures exclusive license from @UCLATDG for advancing lifesaving therapy tdg.ucla.edu/rarity-pbc-sec… #ADASCID #bubblebaby #ucla #lifesaving #genetherapy

UCLATDG's tweet image. #RarityPBC secures exclusive license from @UCLATDG for advancing lifesaving therapy tdg.ucla.edu/rarity-pbc-sec… #ADASCID #bubblebaby #ucla #lifesaving #genetherapy
0
0
2
0
55
ipopi_info's profile picture. IPOPI is the association of Primary Immunodeficiency national patient organisations. Improving awareness, access to early diagnosis and optimal treatments.
IPOPI
@ipopi_info
Jun 8

📢 New IPOPI Hard Talks episode is out! 🧬 Explore ADA-SCID management - from diagnosis to treatment - with Dr Reem Elfeky & Prof Fabio Candotti. 🎥 Watch now: youtu.be/KTi1BXGerZ8 🔬 Sponsored by @ChiesiGroup #IPOPI #HardTalks #ADASCID #RareDisease

ipopi_info's tweet card. IPOPI Hard Talks: Explore ADA-SCID Management – from Diagnosis to...

youtube.com

YouTube

IPOPI Hard Talks: Explore ADA-SCID Management – from Diagnosis to...

Source: youtube.com
0
1
5
0
235
Karen_Pinachyan's profile picture. Shaping the #Future of #Healthcare. MD, ENT surgeon #HealthCareIndustry #DigitalHealth #GeneTherapy #PatientAdvocacy #IBD. PERSONAL ONLY
Daily Dose
@Karen_Pinachyan
Oct 23, 2024

Amazing insightful presentation at #ESGCT2024, brilliantly organized by @ESGCT , by Don Kohn from @Kohn_Lab, on #ADASCID #GeneTherapy history in #PID #PrimaryImmunodeficiency in the session chaired by Claire Booth from @ucl & Jose Carlos Segovia Sanz from Madrid

Karen_Pinachyan's tweet image. Amazing insightful presentation at #ESGCT2024, brilliantly organized by @ESGCT , by Don Kohn from @Kohn_Lab, on #ADASCID #GeneTherapy history in #PID #PrimaryImmunodeficiency in the session chaired by Claire Booth from @ucl & Jose Carlos Segovia Sanz from Madrid
Karen_Pinachyan's tweet image. Amazing insightful presentation at #ESGCT2024, brilliantly organized by @ESGCT , by Don Kohn from @Kohn_Lab, on #ADASCID #GeneTherapy history in #PID #PrimaryImmunodeficiency in the session chaired by Claire Booth from @ucl & Jose Carlos Segovia Sanz from Madrid
Karen_Pinachyan's tweet image. Amazing insightful presentation at #ESGCT2024, brilliantly organized by @ESGCT , by Don Kohn from @Kohn_Lab, on #ADASCID #GeneTherapy history in #PID #PrimaryImmunodeficiency in the session chaired by Claire Booth from @ucl & Jose Carlos Segovia Sanz from Madrid
Karen_Pinachyan's tweet image. Amazing insightful presentation at #ESGCT2024, brilliantly organized by @ESGCT , by Don Kohn from @Kohn_Lab, on #ADASCID #GeneTherapy history in #PID #PrimaryImmunodeficiency in the session chaired by Claire Booth from @ucl & Jose Carlos Segovia Sanz from Madrid
0
0
0
0
101
ChiesiGRD's profile picture. We are making a rare difference.
Chiesi Global Rare Diseases
 @ChiesiGRD
Oct 16, 2024

Our symposium at #ESID2024 will focus on the diagnosis and clinical management of #ADASCID as well as the personal experience of living with immunodeficiency. Learn more: r.chiesi.com/rxcaxbgm @ESIDsociety

0
1
0
0
324
historyatnih's profile picture. Official account of the Office of NIH History and Stetten Museum, National Institutes of Health. We inform, document, and preserve the history of NIH.
NIH History Office
 @historyatnih
Jun 11, 2024

Did you know the first successful gene therapy was done @NIH? Before gene therapy, #ADASCID patients had to receive regular doses of the ADA enzyme, like those pictured here. This recent donation of vials helps us tell the important history of gene therapy.

historyatnih's tweet image. Did you know the first successful gene therapy was done @NIH? Before gene therapy, #ADASCID patients had to receive regular doses of the ADA enzyme, like those pictured here. This recent donation of vials helps us tell the important history of gene therapy.
0
0
2
0
85
humantechnopole's profile picture. The next-generation #lifesciences institute advancing human health through basic research and collaboration.
Human Technopole
 @humantechnopole
Nov 20, 2023

Current therapies address immune issues of the #ADASCID rare genetic disorder, but gaps persist in tackling its neurocognitive challenges. With our @harschnitz and @Telethonitalia's support, we'll use #organoid models to identify new therapeutic targets youtu.be/TYBAtoZekpU

humantechnopole's tweet card. Our Research on the Neuropathology of ADA-SCID with Oliver Harschnitz

youtube.com

YouTube

Our Research on the Neuropathology of ADA-SCID with Oliver Harschnitz

Source: youtube.com
0
1
2
1
885
Kohn_Lab's profile picture. Our mission is to treat patients suffering from primary immunodeficiency diseases with hematopoietic stem cell gene therapy.🩸🦠✂️🧬⛑: tweets from lab members.
The Kohn Lab UCLA
 @Kohn_Lab
Apr 27, 2023

We are all excited for Seersha! #ADASCID

UCLAstemcell's profile picture. Supporting innovation, excellence and the highest ethical standards focused on taking stem cell discoveries from the lab to the patient. (RT≠endorsement)
UCLA Broad Stem Cell
 @UCLAstemcell
Apr 27, 2023

After years of waiting, a little girl born w/ the deadly immune system disorder #ADASCID will finally be receiving a once shelved, lifesaving stem cell gene therapy developed by Dr. Donald Kohn @Kohn_Lab thanks to a group of persistent parents & @CIRMnews. cnn.com/2023/04/27/hea…

UCLAstemcell's tweet card. Later this spring, a little girl in California who essentially has no immune system will receive a lifesaving treatment for “bubble boy disease” thanks to the persistence of a dogged group of...
A drug company abandoned a treatment for  ‘bubble boy disease.’ After a 5-year fight, this little...
Source: cnn.com
0
8
27
0
4K
0
2
9
0
1K
lindawang24's profile picture. Communications @UCLAstemcell // Past: @USCSchPharmacy @NPR, @AP // cat lover allergic to cats
Linda Wang
 @lindawang24
Apr 27, 2023

A hopeful first step for those in the #ADASCID community. Excited for Seersha and her unicorn Cutie Pie to explore this great big world!

UCLAstemcell's profile picture. Supporting innovation, excellence and the highest ethical standards focused on taking stem cell discoveries from the lab to the patient. (RT≠endorsement)
UCLA Broad Stem Cell
 @UCLAstemcell
Apr 27, 2023

After years of waiting, a little girl born w/ the deadly immune system disorder #ADASCID will finally be receiving a once shelved, lifesaving stem cell gene therapy developed by Dr. Donald Kohn @Kohn_Lab thanks to a group of persistent parents & @CIRMnews. cnn.com/2023/04/27/hea…

UCLAstemcell's tweet card. Later this spring, a little girl in California who essentially has no immune system will receive a lifesaving treatment for “bubble boy disease” thanks to the persistence of a dogged group of...
A drug company abandoned a treatment for  ‘bubble boy disease.’ After a 5-year fight, this little...
Source: cnn.com
0
8
27
0
4K
0
0
1
0
204
UCLAstemcell's profile picture. Supporting innovation, excellence and the highest ethical standards focused on taking stem cell discoveries from the lab to the patient. (RT≠endorsement)
UCLA Broad Stem Cell
 @UCLAstemcell
Apr 27, 2023

After years of waiting, a little girl born w/ the deadly immune system disorder #ADASCID will finally be receiving a once shelved, lifesaving stem cell gene therapy developed by Dr. Donald Kohn @Kohn_Lab thanks to a group of persistent parents & @CIRMnews. cnn.com/2023/04/27/hea…

UCLAstemcell's tweet card. Later this spring, a little girl in California who essentially has no immune system will receive a lifesaving treatment for “bubble boy disease” thanks to the persistence of a dogged group of...
A drug company abandoned a treatment for  ‘bubble boy disease.’ After a 5-year fight, this little...
Source: cnn.com
0
8
27
0
4K
DavidJensen's profile picture. Jensen is a retired newsman who has covered the Calif stem cell agency since 2005, publishing more than 5,000 items on his blog, the California Stem Cell Report
David Jensen
 @DavidJensen
Feb 16, 2023

Calif has earmarked $1.5 Billion for research, therapy development/delivery for neurodiseases. Public strategy session set for next week. Diseases mentioned: depression, stroke, Parkinsons, dementia and more. @GreatOrmondSt @Kohn_Lab #ADASCID david293.substack.com/p/strategy-for…

0
0
0
0
23
DavidJensen's profile picture. Jensen is a retired newsman who has covered the Calif stem cell agency since 2005, publishing more than 5,000 items on his blog, the California Stem Cell Report
David Jensen
 @DavidJensen
Jan 12, 2023

Dealing with multimillion-dollar price tags for gene therapies: California may be carving a different pathway. @GreatOrmondSt @Kohn_Lab #ADASCID david293.substack.com david293.substack.com/p/a-california…

0
0
0
0
54
DavidJensen's profile picture. Jensen is a retired newsman who has covered the Calif stem cell agency since 2005, publishing more than 5,000 items on his blog, the California Stem Cell Report
David Jensen
 @DavidJensen
Oct 21, 2022

Want to weigh on who will lead the $12 billion Calif stem cell and gene therapy agency and its priorities? Read this. @GreatOrmondSt @Kohn_Lab #ADASCID @biocomca @UciStemCell @JDRFResearch david293.substack.com/p/public-can-w…

0
0
0
0
0
No results for "#adascid"
Inside_PM's profile picture. Exclusive news, features, and analysis on the research, tools, regulations, and applications driving precision medicine. From the publisher of @GENBio
Inside Precision Medicine
 @Inside_PM
May 12, 2021

2 to 3 Years Later, Gene Therapy Still Helping Patients with #ADASCID. 48 of 50 children who were provided a #genetherapy for the disease ADA-SCID retain replenished immune system function two to three years after receiving their treatment. Read more: ow.ly/DxUL50EL8Fu

Inside_PM's tweet image. 2 to 3 Years Later, Gene Therapy Still Helping Patients with #ADASCID. 48 of 50 children who were provided a #genetherapy for the disease ADA-SCID retain replenished immune system function two to three years after receiving their treatment. Read more: ow.ly/DxUL50EL8Fu
0
4
9
0
0
Kohn_Lab's profile picture. Our mission is to treat patients suffering from primary immunodeficiency diseases with hematopoietic stem cell gene therapy.🩸🦠✂️🧬⛑: tweets from lab members.
The Kohn Lab UCLA
 @Kohn_Lab
May 18, 2022

As Dr. Donald Kohn shares his work on ADA-SCID gene therapy, we want to remind that this clinical trial has resumed with the support of @CIRMnews . We ask for your continuous support as we treat more patients with #ADASCID. #ASGCT2022

Kohn_Lab's tweet image. As Dr. Donald Kohn shares his work on ADA-SCID gene therapy, we want to remind that this clinical trial has resumed with the support of @CIRMnews . We ask for your continuous support as we treat more patients with #ADASCID. #ASGCT2022
0
3
19
0
0
SpringerIME's profile picture. Springer Health+ IME, providing independent medical education in Neurology, Diabetes, Oncology, Rare Diseases, Endocrinology, and Paediatrics.
Springer Health+ IME
 @SpringerIME
Jul 5, 2017

Currently approved & standard of care therapies for ADA-SCID. #deficiency #immunology #ADASCID #raredisease #genetic bit.ly/2tpdo50

SpringerIME's tweet image. Currently approved & standard of care therapies for ADA-SCID. #deficiency #immunology #ADASCID #raredisease #genetic bit.ly/2tpdo50
0
3
0
0
0
SpringerIME's profile picture. Springer Health+ IME, providing independent medical education in Neurology, Diabetes, Oncology, Rare Diseases, Endocrinology, and Paediatrics.
Springer Health+ IME
 @SpringerIME
May 13, 2020

NEW article available Support for using E coli-expressed PEG-ADA for ADA-SCID Read here bit.ly/t-ADA-SCID-art… #ADASCID #RareDisease #Ecoli #infants #PEG #EscherichiaColi

SpringerIME's tweet image. NEW article available Support for using E coli-expressed PEG-ADA for ADA-SCID Read here bit.ly/t-ADA-SCID-art… #ADASCID #RareDisease #Ecoli #infants #PEG #EscherichiaColi
0
0
2
0
0
UCLATDG's profile picture. UCLA Technology Development Group serves as the tech transfer office for the university. Our team bridges academic research to commercialization.
UCLA TDG
 @UCLATDG
Oct 14

#RarityPBC secures exclusive license from @UCLATDG for advancing lifesaving therapy tdg.ucla.edu/rarity-pbc-sec… #ADASCID #bubblebaby #ucla #lifesaving #genetherapy

UCLATDG's tweet image. #RarityPBC secures exclusive license from @UCLATDG for advancing lifesaving therapy tdg.ucla.edu/rarity-pbc-sec… #ADASCID #bubblebaby #ucla #lifesaving #genetherapy
0
0
2
0
55
SpringerIME's profile picture. Springer Health+ IME, providing independent medical education in Neurology, Diabetes, Oncology, Rare Diseases, Endocrinology, and Paediatrics.
Springer Health+ IME
 @SpringerIME
Sep 10, 2018

Newborn Screening for ADA-SCID, A new interactive patient case study from Professor Chiara Azzari. Test your knowledge ada-scid.online/case-studies/n… #diagnose #ADASCID #immunology #RARE #RareDisease #showyourrare #celltherapy #genetherapy #primaryimmunodeficiency #Paediatrics #PID

SpringerIME's tweet image. Newborn Screening for ADA-SCID, A new interactive patient case study from Professor Chiara Azzari. Test your knowledge ada-scid.online/case-studies/n… #diagnose #ADASCID #immunology #RARE #RareDisease #showyourrare #celltherapy #genetherapy #primaryimmunodeficiency #Paediatrics #PID
0
2
1
1
0
SpringerIME's profile picture. Springer Health+ IME, providing independent medical education in Neurology, Diabetes, Oncology, Rare Diseases, Endocrinology, and Paediatrics.
Springer Health+ IME
 @SpringerIME
Nov 27, 2017

"Metabolic, not microbial, pathogenesis likely for ADA-SCID lung disease". New article summary from ada-scid.online #ADASCID #SCID #respiratory #lung #immunodeficiency #metabolic bit.ly/2iW3aoV

SpringerIME's tweet image. "Metabolic, not microbial, pathogenesis likely for ADA-SCID lung disease". New article summary from ada-scid.online #ADASCID #SCID #respiratory #lung #immunodeficiency #metabolic bit.ly/2iW3aoV
0
2
0
0
0
EKFStiftung's profile picture. Die EKFS widmet sich der Förderung medizinischer Forschung und unterstützt medizinisch-humanitäre Projekte. Impressum: https://t.co/ETxaZq2WIJ
Else Kröner-Fresenius-Stiftung
@EKFStiftung
Jun 8, 2020

#EKFSprize20 winner Alessandro Aiuti has made major contributions to a gene therapy for the rare immune disease #ADASCID. Approved as a pharmaceutical remedy in Europe, it is considered one of the most important results of #GeneTherapy development worldwide. #EKFS #healthcare

EKFStiftung's tweet image. #EKFSprize20 winner Alessandro Aiuti has made major contributions to a gene therapy for the rare immune disease #ADASCID. Approved as a pharmaceutical remedy in Europe, it is considered one of the most important results of #GeneTherapy development worldwide. #EKFS #healthcare
0
0
2
1
0
SpringerIME's profile picture. Springer Health+ IME, providing independent medical education in Neurology, Diabetes, Oncology, Rare Diseases, Endocrinology, and Paediatrics.
Springer Health+ IME
 @SpringerIME
Feb 21, 2020

New article available: Chest radiographs may help diagnose ADA-SCID early Read here bit.ly/t-ADA-SCID-art… #RareDiseases #ADASCID #GeneTherapy #rare #Pediatrics #Immunology

SpringerIME's tweet image. New article available: Chest radiographs may help diagnose ADA-SCID early Read here bit.ly/t-ADA-SCID-art… #RareDiseases #ADASCID #GeneTherapy #rare #Pediatrics #Immunology
0
1
0
0
0
SpringerIME's profile picture. Springer Health+ IME, providing independent medical education in Neurology, Diabetes, Oncology, Rare Diseases, Endocrinology, and Paediatrics.
Springer Health+ IME
 @SpringerIME
Mar 22, 2018

Medical education needs you! Please visit New Horizons in the Management of ADA-SCID & share your feedback in a very short survey #diagnose #ADASCID #immunology #RareDisease #showyourrare #celltherapy #genetherapy #primaryimmunodeficiency #Paediatrics #PID bit.ly/2rXEmiP

SpringerIME's tweet image. Medical education needs you! Please visit New Horizons in the Management of ADA-SCID & share your feedback in a very short survey #diagnose #ADASCID #immunology #RareDisease #showyourrare #celltherapy #genetherapy #primaryimmunodeficiency #Paediatrics #PID bit.ly/2rXEmiP
0
1
0
0
0

Something went wrong.


Something went wrong.


United States Trends